In a response to a survey, caregivers of people with spinal muscular atrophy identified the risk of severe adverse events and ...

New ACTG Trial Aims to Control HIV Without the use of ART ...

That led a group of researchers from Australia to explore the possibility of a antifibrotic strategy that would inhibit the pathology in a number of organs. Their findings were published in Science ...

If approved, donidalorsen would be a first-in-class RNA-targeted medicine for hereditary angioedema. The agency’s goal date ...