A breakthrough at the Lagos University Teaching Hospital, Idi-Araba, has brought cheery news to people with sickle cell ...

Wilson celebrates the first U.S. patient to complete gene therapy for sickle cell, but says advocacy must continue.

Skorney cited a drug called Oxbryta from Pfizer (PFE), which was approved to treat the blood disorder sickle cell. Instead of using clinical ... and difficulties with speech. The disease is so rare, ...

For example, Pfizer recently withdrew the sickle cell disease drug Oxbryta from the market, which was the centerpiece of its ...

Q3 2024 Earnings Call Transcript November 13, 2024 Operator: Good morning, and welcome to Fulcrum Therapeutics Third Quarter ...

Andrew Fein, an analyst from H.C. Wainwright, reiterated the Hold rating on Fulcrum Therapeutics (FULC – Research Report). The associated ...

Patient enrollment and site activation progressing in Phase 1b PIONEER trial of pociredir in sickle cell disease (SCD) ― ― Ended the third quarter of 2024 with $257.2 million in cash, cash equivalents ...

The social campaign aimed to defy stigma, give voice to patients and care providers and pave the way for the launch of a ...